Aaron Bean at Veeva explores the challenges of rare diseases: With up to 30 million people in EU living with rare diseases, Veeva discusses the challenges facing these rare diseases

Pharmafile speaks to Chiesi Group: Chiesi Group tells Pharmafile about the challenges facing rare disease research and their hopes for the future of this area

Patient advocacy organisations can form an effective partnership between clinical trials and patients for more efficient trials

The rare disease treatment market has been rapidly changing and receive deserved recognition

Takeda tells Pharmafile about the role of combination treatments in rare diseases, and strategies to make them more accessible

Many advancements have been made within the rare disease field, including gene editing and viral delivery strategies

PHARMAFILE SPEAKS TO The Brain Charity: The Brain Charity explain how they've been providing support to patients with rare diseases throughout the COVID-19 pandemic

Patients play an important but often forgotten role in drug development, this article considers the significance of patient experience while developing treatments

Ipsen tells Pharmafile about the underestimated impacts of rare and ultra-rare diseases

A lack of research, funding and representation for rare diseases can lead to under diagnosis, this article looks to the future of rare disease treatments

Rare and ultra-rare diseases impact a surprising amount of people, this article explores the field of rare diseases as well as the diagnostic journey many patients take